Gene therapy? We are full of hope that Brothers will be able to receive treatment that will stop the effects of this terrible disease.
In addition to the approved drug Elevidys for 4-5 year olds, other drugs with microdystrophin are being researched all the time.
We believe that the Brothers will be given the chance in Europe to receive the drug of the future. Without your support, this stage may be more difficult.
Tymon and Kajetan, two brothers who were born on the 29th of the month. They are following the same road to overcome DMD
Follow the Brothers' progress.
Find out more about DMD - Duchenne Muscular Dystrophy.
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